▎ 摘 要
NOVELTY - Pharmaceutical composition comprises graphene quantum dots as an active ingredient. USE - The pharmaceutical composition is useful for preventing or treating lysosomal storage disease caused by a substrate accumulated in lysosome, inhibiting accumulation of substrate in lysosome and decomposing previously accumulated substrate in an individual. The graphene quantum dots are used for preparing a drug for preventing or treating lysosomal storage disease. The lysosome accumulation disease is chosen from pompe disease, Gauche disease, Fabry disease, GM1-ganglioside accumulation disease, Tay-Sachs disease, Sandhoff disease, Krabbe disease, Farber disease, otitis media, dystrophy, Hurler-Scheie syndrome, Hunter's disease, Sanfilippo syndrome, San Philip's syndrome B, San Philip's syndrome C, San Philip's syndrome D, Morquio's disease A, morquio B syndrome, Maroteaux-Lamy syndrome, sly disease, alpha -mannosidosis, beta -mannosidosis, fucosidosis, sialidosis, Schindler-Kanza disease, and Niemann-Pick disease (all claimed).